In animal models, a gene therapy known as CTx1000 has stopped the progression of both frontotemporal dementia and amyotrophic lateral sclerosis. Researchers studying neurology at Macquarie University in Australia have…
GENE THERAPY
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Hepatocellular carcinoma (HCC) in mice can be reduced via gene therapy, according to a study from the UC Davis Comprehensive Cancer Center (California, USA). This is achieved by inhibiting a…
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Ιn a world first, the UK medicines regulator has approved a therapy that uses the CRISPR–Cas9 gene-editing tool as a treatment. The therapy, called Casgevy, will treat the blood conditions…
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The first trial in humans of the precise gene-editing technique known as base editing, by using the CRISPR–Cas9 machinery, has shown promising results for keeping cholesterol levels in check. The…
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The scientists from Nuffield Department of Clinical Neurosciences assessed if a tailored pain treatment approach could involve directly inhibiting pain-related hyperactivity in sensory neurons. Indeed, they have now shown that…
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A research group from the University of Barcelona and the Physiopathology of Obesity and Nutrition Networking Biomedical Research Centre (CIBERobn) (Spain) has developed a strategy to fight obesity and diabetes…
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A recent study has shown for the first time that gene therapy can successfully restore hearing in an aged mouse model of human genetic deafness, demonstrating the feasibility of gene…

