The Long-Awaited Three-Year Study Results on Huntington’s Disease AMT-130, uniQure’s gene therapy, would be the first genetic treatment for Huntington’s disease, if approved. The observed slowing of disease progression is…
ΓΟΝΙΔΙΑΚΗ ΘΕΡΑΠΕΙΑ
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A large research group led by Dr. Jeff Vierstra, a researcher at the Altius Institute for Biomedical Sciences in Seattle (USA), and Dr. Nikoletta Psatha, Assistant Professor in the Department…
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Scientists at Trinity College Dublin have developed a very promising gene therapy to treat glaucoma, a debilitating eye condition that affects around 80 million people globally and can result in…
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Children’s Hospital of Philadelphia (USA) corrected genetic hearing loss using a gene therapy procedure developed in Italy. An 11-year-old kid with a rare type of congenital deafness has been able…
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In animal models, a gene therapy known as CTx1000 has stopped the progression of both frontotemporal dementia and amyotrophic lateral sclerosis. Researchers studying neurology at Macquarie University in Australia have…