Once a death sentence, hemophilia may soon have a treatment. A hereditary condition that primarily affects boys is caused by blood clotting failure. After an injury, hemophilia can result in sudden, severe bleeding. There were only measures to halt the bleeding twenty years ago. Gene therapies now have even greater hope of treating this illness in the future.
More info:
1) Hemophilia Emerging Therapies – January 2024
2) De Wolf D, Singh K, Chuah MK, VandenDriessche T. Hemophilia Gene Therapy: The End of the Beginning? Hum Gene Ther. 2023 Sep;34(17-18):782-792. doi: 10.1089/hum.2023.112. PMID: 37672530.
3) https://www.ivanhoe.com/medical-breakthroughs/gene-therapy-redefining-hemophilia-treatment/
4) Νews from the International Society on Thrombosis and Haemostasis (ISTH)
Gene Therapy in Hemophilia
An ISTH Education Initiative
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